Working toward a world free of rare diseases

01 Science leading

Advancing research to develop therapeutics for rare diseases

There are over 10,000 rare diseases, yet less than 5% of them have effective treatments. We collaborate with research teams, families, and advocacy organizations from around the world to work toward treatments and improve patient access to affordable care.

02 Community building

Impacting our local communities by supporting health-based initiatives and community development

We are committed to supporting underserved communities. We build partnerships with community-based organizations to respond to the urgent public health needs of our neighbors. 

03 Research Institute

Developing therapies for those ultra-rare diseases that lack commercial potential

In addition to providing funding to labs conducting research on rare diseases, we have our own lab dedicated to advancing promising therapeutics. This work is driven by the promise of patient impact, not financial returns.

04 Policy Institute

Highlighting the value of medical innovation

Science has incredible potential to impact lives, but without the right policies and education these innovations may never reach patients. Through education and advocacy, we aim to support equitable access to medical innovation for patients around the world. 

RTW Charitable Foundation in numbers


Rare disease grants awarded across 6 countries


Community organizations and research partners have been supported in responding to COVID needs in New York City

About us

Our mission is to power rare disease research, medical innovation and humanitarian collaborations to improve the health of underserved communities.

Grant programs


Our ultra rare disease research grant program seeks to move early science forward to therapeutic development.

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Our NYC community grant program seeks to meet the urgent challenges of our most under-resourced communities.

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